86本のエピソード
MyFSHD Peter L Jones, PhD
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- ビジネス
MyFSHD is about education and personal empowerment for the worldwide facioscapulohumeral muscular dystrophy (FSHD) community. Here we have discussions and commentary hosted by FSHD researcher Peter Jones, PhD, on many things of interest to the FSHD community. Learn about the science behind the different FSHD therapeutic approaches, FSHD pathology, family genetics and FSHD diagnostics. We will discuss upcoming clinical trials and what to look forward to. You will get to understand how you can be better prepared, become involved, and help contribute to defeating FSHD once and for all.
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A FORTITIDE follow-up with our (not so) Angry Dad.
"There's a time for daring and there's a time for caution, and a wise man understands which is called for." Brad our Angry Dad is back with some questions for us on the Avidity FORTITUDE AOC 1020 phase 1/2 trial interim data report and some muscle building.
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Send in a voice message: https://podcasters.spotify.com/pod/show/peter-l-jones/message -
A(+) is still for Avidity: give me the good stuff!
"Whatchyou talkin' 'bout Willis?" In a field where every press release is met with unsubstantiated hoopla and proclamations of BREAKTHROUGH! to fire you up to shake you down, we finally have some real news. We provide our evaluation of Avidity's public interim report on their FORTITUDE AOC-1020 phase 1/2 trial.
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Send in a voice message: https://podcasters.spotify.com/pod/show/peter-l-jones/message -
Pigs and p38
"You're messing with the wrong guy!!!!" We expand a bit more on the utility of the FSHD-like pig model and then discuss the science behind and implications of p38 inhibition for FSHD.
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Send in a voice message: https://podcasters.spotify.com/pod/show/peter-l-jones/message -
The three little (FSHD) piggies.
"We don't get a lot of things to really care about." So, you think you are interested in science, eh? Well, let's see how the sausage is made. Today we share our experience generating the FSHD-like minipig models, which will be key tools for testing and advancing better FSHD therapeutics and developing methods for building back your muscles.
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Send in a voice message: https://podcasters.spotify.com/pod/show/peter-l-jones/message -
CRISPR in the clinic
"Come out to the coast, we'll get together, have a few laughs..." The holiday season we discuss the recent FDA approved CRISPR therapy for sickle cell disease and some dynamics of methylation.
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Send in a voice message: https://podcasters.spotify.com/pod/show/peter-l-jones/message -
Allow me to reintroduce Jaegerthekidd
"As I leave my competition respirator style, climb the ladder to success escalator style." Today we have the Jaegercast, but first we continue our discussion about apabetalone, a new candidate drug for FSHD.
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Send in a voice message: https://podcasters.spotify.com/pod/show/peter-l-jones/message